112. Thalassemia and Globin Gene Regulation: Poster III

Efficacy of mitapivat in patients with transfusion dependent alpha thalassemia Subgroup analysis from the ENERGIZE T trial

Snh 119014 a novel pyruvate kinase activator enhances ATP production and reduces oxidative stress in erythroid cells from patients with β thalassemia major

Long term transfusion free duration and impact on transfusion related burdens Results from the ongoing ENERGIZE T open label extension study of mitapivat in transfusion dependent alpha or beta thalassemia

Thalassemia in europe A cross border real world data analysis from the radeep registry

Impact of long term luspatercept treatment on iron parameters in patients with transfusion dependent and non transfusion dependent β thalassemia Results from the phase 3b long term follow up study

Developing β thalassemia mouse model by deleting hbb genes for therapeutic evaluation

A phase 2 study of luspatercept in adults and adolescents with α thalassemia Findings from the dose confirmation cohort in adolescents