801. Gene Therapies: Poster II

Impact of Glycine-Serine Linker on Target Antigen Binding and Subsequent CD37CAR-T Performance

GO-8: Stable Expression of Factor VIII over 5 Years Following Adeno-Associated Gene Transfer in Subjects with Hemophilia a Using a Novel Human Factor

Phenotypic HSPC Rescue By RNA Lipid Nanoparticles in a Murine Model of Fanconi Anemia

Phosphorus Disruption Is Associated with the Incidence and Severity of Neurotoxicity Symptoms in CD19-Targeted CAR-T Cell Therapy: A Pooled Clinical T

Using Inducible Signaling Receptors to Increase Erythropoietic Output from Genome-Edited Hematopoietic Stem Cells

Health-Related Quality of Life in Adults with Hemophilia B after Receiving Gene Therapy with Fidanacogene Elaparvovec

Significant Cytokine Release Syndrome Risk Model with T-Cell Engaging Therapies

In Vitro and In Vivo Specificity and Biodistribution of a Novel CD8-Targeted Fusosome

Feasibility of Extracorporeal Delivery of Fusosomes to Generate CAR T Cells In Vivo